Long School of Medicine

Team eyes gene therapy for children paralyzed by rare mutations

<p>Turning on the gene in mice restores the animals’ motor functions The 50 families stretch from the Netherlands and the United Kingdom to the United States and China. Each family has a child who is paralyzed from a mutation in a single gene named Contactin-Associated Protein 1 (Cntnap1). The children are locked inside their bodies, [&hellip;]</p>

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